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Two-phase outcome-dependent studies for failure times and testing for effects of expensive covariates

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  • J. F. Lawless

    (University of Waterloo)

Abstract

Two- or multi-phase study designs are often used in settings involving failure times. In most studies, whether or not certain covariates are measured on an individual depends on their failure time and status. For example, when failures are rare, case–cohort or case–control designs are used to increase the number of failures relative to a random sample of the same size. Another scenario is where certain covariates are expensive to measure, so they are obtained only for selected individuals in a cohort. This paper considers such situations and focuses on cases where we wish to test hypotheses of no association between failure time and expensive covariates. Efficient score tests based on maximum likelihood are developed and shown to have a simple form for a wide class of models and sampling designs. Some numerical comparisons of study designs are presented.

Suggested Citation

  • J. F. Lawless, 2018. "Two-phase outcome-dependent studies for failure times and testing for effects of expensive covariates," Lifetime Data Analysis: An International Journal Devoted to Statistical Methods and Applications for Time-to-Event Data, Springer, vol. 24(1), pages 28-44, January.
    • Handle: RePEc:spr:lifeda:v:24:y:2018:i:1:d:10.1007_s10985-016-9386-8
    DOI: 10.1007/s10985-016-9386-8
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    Cited by:

    1. Douglas E. Schaubel & Bin Nan, 2018. "Special issue dedicated to Jack Kalbfleisch," Lifetime Data Analysis: An International Journal Devoted to Statistical Methods and Applications for Time-to-Event Data, Springer, vol. 24(1), pages 1-2, January.
    2. Soave, David & Lawless, Jerald F., 2023. "Regularized regression for two phase failure time studies," Computational Statistics & Data Analysis, Elsevier, vol. 182(C).
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    4. Bryan E. Shepherd & Kyunghee Han & Tong Chen & Aihua Bian & Shannon Pugh & Stephany N. Duda & Thomas Lumley & William J. Heerman & Pamela A. Shaw, 2023. "Multiwave validation sampling for error‐prone electronic health records," Biometrics, The International Biometric Society, vol. 79(3), pages 2649-2663, September.

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